FDA approves gene-editing therapy for sickle cell disease

The FDA approved gene-editing therapy Casgevy to treat sickle cell disease. Developed by Vertex Pharmaceuticals (VRTX) and CRISPR Therapeutics (CRSP), the one-time treatment harnesses gene editing advancements. Vertex CEO Dr. Reshma Kewalramani says the approach involves extracting a patient’s stem cells, correcting the defect in those cells using CRISPR gene editing tools, then re-infusing the edited cells into the patient - relieving painful symptoms. Patients who undergo this $2.2 million procedure may eliminate painful sickle cell crises called VOC’s. Kewalramani contrasts the cost against the $4-6 million lifetime price tag for conventional sickle cell management. #youtube #genetics #yahoofinance About Yahoo Finance: Yahoo Finance provides free stock ticker data, up-to-date news, portfolio management resources, comprehensive market data, advanced tools, and more information to help you manage your financial life. - Get the latest news and data at - Download the Yahoo Finance app on Apple () or Android () - Follow Yahoo Finance on social: X: Instagram: TikTok: @yahoofinance?lang=en Facebook: LinkedIn: